Progress in spinal muscular atrophy research

Erstveröffentlichung
2022Authors
Wurster, Claudia
Petri, Susanne
Wissenschaftlicher Artikel
Published in
Current Opinion in Neurology ; 35 (2022), 5. - S. 693-698. - ISSN 1350-7540. - eISSN 1473-6551
Link to publication
https://dx.doi.org/10.1097/WCO.0000000000001102Institutions
UKU. Klinik für NeurologieSubject headings
[Free subject headings]: clinical and basic research | new therapies | spinal muscular atrophy | SURVIVAL MOTOR-NEURON | ONASEMNOGENE ABEPARVOVEC | NUSINERSEN TREATMENT | SINGLE NUCLEOTIDE | GENE-THERAPY | SHAM CONTROL | MOUSE MODEL | OPEN-LABEL | PART 1 | RISDIPLAM[DDC subject group]: DDC 610 / Medicine & health