| Author | Moscatelli, Ilana | dc.contributor.author |
| Author | Almarza, Elena | dc.contributor.author |
| Author | Schambach, Axel | dc.contributor.author |
| Author | Ricks, David | dc.contributor.author |
| Author | Schulz, Ansgar | dc.contributor.author |
| Author | Herzog, Christopher D. | dc.contributor.author |
| Author | Henriksen, Kim | dc.contributor.author |
| Author | Askmyr, Maria | dc.contributor.author |
| Author | Schwartz, Jonathan D. | dc.contributor.author |
| Author | Richter, Johan | dc.contributor.author |
| Date of accession | 2021-04-16T06:54:27Z | dc.date.accessioned |
| Available in OPARU since | 2021-04-16T06:54:27Z | dc.date.available |
| Date of first publication | 2021 | dc.date.issued |
| Language | en | dc.language.iso |
| Publisher | Universität Ulm | dc.publisher |
| Keyword | STEM-CELL TRANSPLANTATION | dc.subject |
| Keyword | AUTOSOMAL RECESSIVE OSTEOPETROSIS | dc.subject |
| Keyword | SEVERE COMBINED IMMUNODEFICIENCY | dc.subject |
| Keyword | BONE-MARROW-TRANSPLANTATION | dc.subject |
| Keyword | CHRONIC GRANULOMATOUS-DISEASE | dc.subject |
| Keyword | LENTIVIRAL VECTOR | dc.subject |
| Keyword | CHLORIDE CHANNEL | dc.subject |
| Keyword | PROTON PUMP | dc.subject |
| Keyword | OSTEOCLAST | dc.subject |
| Keyword | RESORPTION | dc.subject |
| Dewey Decimal Group | DDC 610 / Medicine & health | dc.subject.ddc |
| Title | Gene therapy for infantile malignant osteopetrosis: review of pre-clinical research and proof-of-concept for phenotypic reversal | dc.title |
| Resource type | Wissenschaftlicher Artikel | dc.type |
| Institution | UKU. Klinik für Kinder- und Jugendmedizin | uulm.affiliationSpecific |
| DCMI Type | Text | uulm.typeDCMI |
| Category | Publikationsnachweise | uulm.category |
| DOI (external) | 10.1016/j.omtm.2020.12.009 | dc.identifier.doiExternal |
| Source - Title of source | Molecular Therapy - Methods and Clinical Development | source.title |
| Source - Place of publication | Cell Press | source.publisher |
| Source - Volume | 20 | source.volume |
| Source - Year | 2021 | source.year |
| Source - From page | 389 | source.fromPage |
| Source - To page | 397 | source.toPage |
| Source - eISSN | 2329-0501 | source.identifier.eissn |
| Open Access | DOAJ Gold, Green Published | uulm.OA |
| Community | Universitätsklinikum Ulm | uulm.community |
| WoS | 000629246400033 | uulm.identifier.wos |
| Bibliography | uulm | uulm.bibliographie |
