Clinical benefit of eculizumab in patients with no transfusion history in the International Paroxysmal Nocturnal Haemoglobinuria Registry

Erstveröffentlichung
2017Authors
Almeida, Antonio M.
Bedrosian, Camille
Cole, Alexander
Muus, Petra
Schrezenmeier, Hubert
Wissenschaftlicher Artikel
Published in
Internal Medicine Journal ; 47 (2017), 9. - S. 1026-1034. - ISSN 1444-0903. - eISSN 1445-5994
Link to publication
https://dx.doi.org/10.1111/imj.13523Institutions
Institut für Klinische Transfusionsmedizin und Immungenetik Ulm gGmbH (IKT)Subject headings
[Free subject headings]: paroxysmal nocturnal haemoglobinuria | eculizumab | transfusion | high disease activity | outcome | complement inhibitor eculizumab | thrombosis | validation[DDC subject group]: DDC 610 / Medicine & health